Clinical Trials for Wiskott-Aldrich Syndrome

Clinical trials are research studies conducted in an effort to improve overall patient health and care. Each trial involves running supervised tests to determine the effectiveness and safety of new drugs, procedures and/or devices with the aim of answering scientific questions about a disease or condition. Risks and side-effects are also evaluated during these trials with results ranging from being unpleasant, with side effects such as headaches, to more serious or even life-threatening risks. A clinical trial may be separated into phases, or steps, with each step designed to answer a separate research question. This maybe reflected in the trial name.

A brief description of each phase:

• Phase I: Usually designed to evaluate safety, determine a safe dosage range, and identify side effects on a small group of patients.
• Phase II: If Phase I is successful, the trial is then repeated with a larger group to further evaluate its effect and safety.
• Phase III: Trials are conducted on an ever larger group and are compared with the best current treatment while gathering more information on effect and safety.
• Phase IV: These studies monitor long-term side effects after the treatment has been marketed.

Clinical Trials data for Wiskott-Aldrich Syndrome is grouped into the following categories:-

• View by trial name
• View by drugs used in Wiskott-Aldrich Syndrome clinical trials

Clinical Trials by trial name

The format for each of the following is:

• The name of the trial,
• followed by whether the trial is recruiting patients,
  - The trial may not have started and not yet recruiting, or the trial may have started and do not need any more recruitements, or the trial may be completed.
  - Note**: Please follow the link to determine the current trial status.
• followed by a list of drug/s, if any, used in the trial

ClinicalTrials.gov has listed the following trials for Wiskott-Aldrich Syndrome:

• Study of Genetic and Molecular Defects in Primary Immunodeficiency Disorders - This study is no longer recruiting patients (Current: 23 Nov 2006)
• Allogeneic Bone Marrow Transplantation in Patients With Primary Immunodeficiencies - This study is no longer recruiting patients (Current: 23 Nov 2006) - anti-thymocyte globulin,busulfan,cyclophosphamide,cyclosporine,etoposide,methotrexate,methylprednisolone,prednisone
• Pilot Study of Allogeneic Bone Marrow Transplantation Plus Cyclosporine and Mycophenolate Mofetil to Induce Mixed Hematopoietic Chimerism in Patients With Primary T-Cell Immunodeficiency Disorders - This study is currently recruiting patients (Current: 23 Nov 2006) - cyclosporine,mycophenolate mofetil
• Haploidentical Hematopoietic Stem Cell Transplantation (HSCT) for Pediatric Patients With Wiskott-Aldrich Syndrome: A Pilot Study - This study is currently recruiting patients (Current: 23 Nov 2006)
• Efficacy, Safety and Pharmacokinetics of Gammaplex in Primary Immunodeficiency Diseases. - This study is currently recruiting patients (Current: 23 Nov 2006) - Intravenous immunoglobulin
• Rapid Infusion of Immune Globulin Intravenous (Human) In Primary Immunodeficiency Patients - This study has been completed (Current: 23 Nov 2006) - Immune Globulin Intravenous (Human) , 10%
• Molecular and Clinical Studies of Primary Immunodeficiency Diseases - This study is currently recruiting patients (Current: 23 Nov 2006)
• Study of Megakaryocytes From Patients With Abnormal Platelet Vesicles - This study is currently recruiting patients (Current: 23 Nov 2006)

Drugs used in Clinical Trials for Wiskott-Aldrich Syndrome

The format for each of the following is:

• The drug,
• followed by the name of the trial,
• followed by whether the trial is recruiting patients,
  - The trial may not have started and not yet recruiting, or the trial may have started and do not need any more recruitements, or the trial may be completed.
  - Note**: Please follow the link to determine the current trial status.

ClinicalTrials.gov has listed the following drugs in trials for Wiskott-Aldrich Syndrome:

• Anti-Thymocyte Globulin - Allogeneic Bone Marrow Transplantation in Patients With Primary Immunodeficiencies - This study is no longer recruiting patients (Current: 23 Nov 2006)
• Busulfan - Allogeneic Bone Marrow Transplantation in Patients With Primary Immunodeficiencies - This study is no longer recruiting patients (Current: 23 Nov 2006)
• Cyclophosphamide - Allogeneic Bone Marrow Transplantation in Patients With Primary Immunodeficiencies - This study is no longer recruiting patients (Current: 23 Nov 2006)
• Cyclosporine - Allogeneic Bone Marrow Transplantation in Patients With Primary Immunodeficiencies - This study is no longer recruiting patients (Current: 23 Nov 2006)
• Cyclosporine - Pilot Study of Allogeneic Bone Marrow Transplantation Plus Cyclosporine and Mycophenolate Mofetil to Induce Mixed Hematopoietic Chimerism in Patients With Primary T-Cell Immunodeficiency Disorders - This study is currently recruiting patients (Current: 23 Nov 2006)
• Etoposide - Allogeneic Bone Marrow Transplantation in Patients With Primary Immunodeficiencies - This study is no longer recruiting patients (Current: 23 Nov 2006)
• Immune Globulin Intravenous (Human) , 10% - Rapid Infusion of Immune Globulin Intravenous (Human) In Primary Immunodeficiency Patients - This study has been completed (Current: 23 Nov 2006)
• Intravenous immunoglobulin - Efficacy, Safety and Pharmacokinetics of Gammaplex in Primary Immunodeficiency Diseases. - This study is currently recruiting patients (Current: 23 Nov 2006)
• Methotrexate - Allogeneic Bone Marrow Transplantation in Patients With Primary Immunodeficiencies - This study is no longer recruiting patients (Current: 23 Nov 2006)
• Methylprednisolone - Allogeneic Bone Marrow Transplantation in Patients With Primary Immunodeficiencies - This study is no longer recruiting patients (Current: 23 Nov 2006)
• Mycophenolate Mofetil - Pilot Study of Allogeneic Bone Marrow Transplantation Plus Cyclosporine and Mycophenolate Mofetil to Induce Mixed Hematopoietic Chimerism in Patients With Primary T-Cell Immunodeficiency Disorders - This study is currently recruiting patients (Current: 23 Nov 2006)
• Prednisone - Allogeneic Bone Marrow Transplantation in Patients With Primary Immunodeficiencies - This study is no longer recruiting patients (Current: 23 Nov 2006)

The trial data on this page has been sourced from

• The U.S. National Library of Medicine (NLM) together with ClinicalTrials.gov

Rate This Website

What do you think about the features of this website? Take our user survey and have your say:

Website User Survey

Medical Tools & Articles:

Next articles:

• External links relating to Wiskott-Aldrich Syndrome
• THROMBOCYTOPENIA (Algorithmic Diagnosis of Symptoms and Signs)
• Thrombocytopenia (In A Page: Pediatric Signs and Symptoms)
• THROMBOCYTOPENIA (Differential Diagnosis in Primary Care)
• Thrombocytopenia (A Pocket Manual of Differential Diagnosis)

Tools & Services:

• Bookmark this page
• Take a survey relating to Wiskott-Aldrich Syndrome
• Symptom Search
• Symptom Checker
• Medical Dictionary
• Give your feedback

Medical Articles:

• Disease & Treatments Search
• Misdiagnosis Center
• Full list of interesting articles

Forums & Message Boards

• Ask or answer a question at the Boards:
• I cannot get a diagnosis. Please help.
• Tell us your medical story.
• Share your misdiagnosis story.
• What is the best treatment for my condition?
• See all the Boards.

Enter your search terms Submit search form
Search The Web Search wrongdiagnosis.com

Common Health Mistakes

Symptom
Checker

Search Specialists by State and City